Patient Advocacy

Partnering with Patients to Shape Every Step of Care, Discovery, and Progress.

At Amicus, the lived experiences of patients guide how we think, act, and innovate — every day.

From Our Chief Patient Officer

At Amicus, our mission begins and ends with the people living with rare diseases — patients, caregivers, families, and the communities that support them.

Across every function, all around the world, we are building lasting relationships that help us understand what matters most to patients, caregivers, and families, whose voices and lived experiences are not only heard but also meaningfully integrated into how we design therapies, shape programs, and measure success.

We are immensely grateful to the rare disease community and families living with Pompe disease, Fabry, and FSGS for their willingness to share their experiences and expertise with us.

Every conversation helps us see our work through the eyes of people living with and caring for those affected by rare disease, driving our mission to develop and deliver transformative therapies—faster—and to support people and families in the moments that matter most.
 

Tiffany Patrick

Chief Patient Officer

Resources

For information on Pompe disease, please refer to the following resources:

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