Amicus Therapeutics Expanded Access Policy

Expanded Access to Amicus Investigational Drugs

Expanded Access Program (EAP)

Since the company’s earliest days, extraordinary dedication to people affected by rare and orphan diseases has been a hallmark of Amicus Therapeutics. Our mission is to develop new medicines that improve the health and well-being of people living with rare diseases. With the development of medicines designed to satisfy unmet medical needs, comes the promise that these medicines will be broadly accessible.

Click on the link in the right-hand navigation panel to access our EAP policy

Key Contacts

Patients, their families and caregivers seeking general information may reach out to Amicus’ Global Patient & Professional Advocacy Department at patientadvocacy@amicusrx.com or call toll-free in the United States and Canada at 1-866-9AMICUS
(1-866-926-4287)

Make a Request

Physicians or qualified healthcare providers (HCP) may submit a request by completing the following intake forms:

Pompe EAP intake form
Fabry EAP intake form

NP-NN-ALL-00020421

Rare Stories

Be inspired by people living with rare diseases across the globe.

Noah, Age 10

Living with Pompe Disease

Katelynn, Age 10

Living with CDKL5 Deficiency Disorder (CDD)

Kiera, Age 14