Noah, Age 10
Living with Pompe Disease
Since the company’s earliest days, extraordinary dedication to people affected by rare and orphan diseases has been a hallmark of Amicus Therapeutics. Our mission is to develop new medicines that improve the health and well-being of people living with rare diseases. With the development of medicines designed to satisfy unmet medical needs, comes the promise that these medicines will be broadly accessible.
Click on the link in the right-hand navigation panel to access our EAP policy
Patients, their families and caregivers seeking general information may reach out to Amicus’ Global Patient & Professional Advocacy Department at patientadvocacy@amicusrx.com or call toll-free in the United States and Canada at 1-866-9AMICUS
(1-866-926-4287)
Physicians or qualified healthcare providers (HCP) may submit a request by completing the following intake forms:
NP-NN-ALL-00020421
Be inspired by people living with rare diseases across the globe.