About Us

Redefining Expectations in Rare Diseases

Amicus Therapeutics is a leading global rare-disease focused biotechnology company with a clear and compelling mission: to develop and deliver transformative medicines for people living with rare diseases.

We believe that breakthroughs are possible. That is why we push ideas as far and as fast as possible – in our science, in our work with patients, in everything we do – because every moment matters when you are living with a rare disease.

Amicus: Created for Patients with Rare Disease, with Patients with Rare Disease

Founded in 2002, Amicus was created for patients and with patients.

In 2005, under the leadership of then-CEO and rare disease parent John Crowley, the entire company came together to create three founding beliefs.

We Believe…
In the Fight to Remain at the Forefront of Therapies for Rare and Orphan Diseases
  • We seek to deliver the highest quality therapies for persons living with these diseases
  • We support the disease communities – and their families
  • We are passionate about what we do
  • We encourage and embrace constant innovation
  • We have a duty to obsolete our own technologies
  • We push ideas as far and as fast as possible
  • We take smart risks
  • We work hard
  • We keep asking the tough questions
  • We will never be constrained by prior thinking
  • We learn from our mistakes
  • We think differently – very differently
We Believe…
In Our Future to Build Long-term Value for Our Stakeholders
  • We are all owners of this business
  • We are business led and science driven
  • Maximizing value for our shareholders is the foundation of our future successes
  • Our medicines must be fairly priced and broadly accessible
  • We build strategic partnerships
  • We will not lie, cheat or steal
  • We take full responsibility for our actions
We Believe…
In Each Other to Foster Teamwork and Respect for Each Individual’s Contribution
  • Our passion for making a difference unites us
  • We value an inclusive environment where individual experiences and perspectives are celebrated, and voices from the rare disease community are heard.
  • We communicate openly, honestly and respectfully
  • Our families are part of the Amicus experience
  • Work-life balance keeps us healthy
  • We listen
  • We have fun

Guided by these founding beliefs and inspired by the patients who are the heart of everything we do, our company has become one of the leading rare-disease focused biotech companies.

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Noah, Age 10
Noah, Age 10

Living with Pompe Disease
Hiroki, Age 26

Living with Pompe Disease
Sam, Age 37

Living with Pompe Disease